4th Edition of International Precision Medicine Conference

August 17-19, 2023 | Online Event

August 17-19, 2023 | Online Event

Rare Diseases/Disorders and Orphan Drugs

Rare Diseases/Disorders and Orphan Drugs

Rare diseases are frequently life-threatening, chronic illnesses. A rare disease is defined by the World Health Organization as a debilitating lifelong disease or disorder with a prevalence of 1 or less per 1000 people. Different countries, on the other hand, have their own definitions tailored to their individual needs and in the context of their population, health-care system, and resources. Medications developed specifically to treat rare disorders, known as "orphan drugs," are frequently left underdeveloped economically because of the minimal prospect for profit. Rare Diseases and Orphan Drugs demonstrates that studying rare diseases has led to much of what we currently know about common diseases. It posits that our rapid development in the field of rare diseases will lead to future advancements in the prevention, diagnosis, and treatment of common diseases. Rare disorders, on the other hand, are frequently caused by mutations in a single gene.

  • FDA approved drugs
  • Efficacy of orphan drugs
  • Rare Drug Market
  • Precision Medicine in Rare Disease
Committee Members
Speaker at International Precision Medicine Conference 2023 - Bernd Blobel

Bernd Blobel

University of Regensburg, Germany
Speaker at International Precision Medicine Conference 2023 - Roy Gary Beran

Roy Gary Beran

University of New South Wales, Australia
Speaker at International Precision Medicine Conference 2023 - Matthias Schwab

Matthias Schwab

University of Tubingen, Germany
2023 Speakers Speakers
Speaker at International Precision Medicine Conference 2023 - Thomas Webster

Thomas Webster

Interstellar Therapeutics, United States
Speaker at International Precision Medicine Conference 2023 - Boris Tankhilevich

Boris Tankhilevich

Magtera, Inc., United States
Speaker at International Precision Medicine Conference 2023 - Isabella Friis Jorgensen

Isabella Friis Jorgensen

University of Copenhagen, Denmark
Speaker at International Precision Medicine Conference 2023 - Guo Wei He

Guo Wei He

Tianjin University, China

Submit your abstract Today

Watsapp